Exondys 51 FDA Approved Drugs
EXONDYS 51 [Eteplirsen]
RX
- 100mg/2ml (50mg/ml) (iv (infusion) solution)
500mg/10ml (50mg/ml) (iv (infusion) solution)
Sarepta Theraps IncSep 19, 2016
- (i)treatment of duchenne muscular dystrophy; (ii)restoring/increasing functional dystrophin protein; or (iii) inducing skipping; each of (i)-(iii) in patients having a confirmed mutation of the dmd gene that is amenable to exon 51 skipping.
- Restoring an mrna reading frame to induce dystrophin protein production in patients having a mutation of the dmd gene that is amenable to exon 51 skipping.
- Treatment of duchenne muscular dystrophy in patients having a mutation of the dmd gene that is amenable to exon 51 skipping.
WARNING: Consult a licensed physician in the appropriate field for medical treatment and drug prescription. Do not self medicate.